A Phase 3b, Single Arm, Open-label Study to Evaluate the Efficacy and Safety of BMN 270, an Adeno-Associated Virus Vector-Mediated Gene Transfer of Human Factor VIII, with Prophylactic Corticosteroids in Hemophilia A Patients.

  • Tran, Huyen (Primary Chief Investigator (PCI))
  • Kennedy, Nola (Project Manager)

Project: Research

Project Details

StatusActive
Effective start/end date2/12/20 → 31/12/25

Keywords

  • Blood diseases
  • Haemophilia
  • Clinical trial

Clinical Trial Phase

  • Phase III (a & b)