A Phase 3b, Single Arm, Open-label Study to Evaluate the Efficacy and Safety of BMN 270, an Adeno-Associated Virus Vector-Mediated Gene Transfer of Human Factor VIII, with Prophylactic Corticosteroids in Hemophilia A Patients.

  • Tran, Huyen (Primary Chief Investigator (PCI))
  • Kennedy, Nola (Project Manager)

Project: Research

Project Details

Effective start/end date2/12/2031/12/25


  • Blood diseases
  • Haemophilia
  • Clinical trial