A Phase 3 Open-Label, Single-Arm Study to Evaluate The Efficacy and Safety of BMN 270, an Adeno-Associated Virus Vector-Mediated Gene Transfer of Human Factor VIII in Hemophilia A patients with Residual FVIII Levels < 1 IU/dL Receiving Prophylactic FVIII Infusions.

  • Tran, Huyen (Primary Chief Investigator (PCI))
  • Kennedy, Nola (Project Manager)

Project: Research

Project Details

Effective start/end date1/10/1931/12/24


  • Malignant Haematology
  • Haemophilia
  • Clinical trial