A Phase 2a, Randomized, Open-Label Study to Evaluate the Efficacy, Safety, Tolerability, Pharmacokinetics and Pharmacodynamics of ISIS 702843 Administered Subcutaneously to Patients with Non-Transfusion Dependent β-Thalassemia Intermedia

Project: Research

Project Details

StatusActive
Effective start/end date5/05/204/05/25

Keywords

  • clinical trial
  • phase 2 study
  • thalassaemia
  • treatment efficacy
  • treatment safety