A Phase 1/2a Dose-Escalating Study to Evaluate the Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of ARO-DUX4 in Adult Patients with Facioscapulohumeral Muscular Dystrophy Type 1

  • Rodrigues, Joseph (Primary Chief Investigator (PCI))

Project: Research

Project Details

StatusActive
Effective start/end date17/04/25 → 16/04/27

Keywords

  • Clinical Trials
  • ARODUX4-1001
  • ARO-DUX4

Clinical Trial Phase

  • Phase I